Search for Clinical Trial Results
Glycogen Storage Disease - 49 Studies Found
Status | Study |
Recruiting |
Study Name: A Long Term Follow up Study in Late-onset Pompe Disease Condition: Pompe Disease Date: 2008-07-09 |
Recruiting |
Study Name: A Pilot Study of Pyridostigmine in Pompe Disease Condition: Pompe Disease Date: 2015-01-23 Interventions: Drug: Pyridostigmine Bromide Pyridostigmine is an acetylcholinesterase inhibitor, which increases the am |
Recruiting |
Study Name: A Natural History Study of Adult Onset Pompe Disease Using Muscle MRI Condition: Pompe Disease Date: 2013-07-31 |
Completed |
Study Name: Albuterol in Individuals With Late Onset Pompe Disease (LOPD) Condition: Pompe Disease Date: 2013-05-08 Interventions: Drug: Albuterol Albuterol 4 mg |
Completed |
Study Name: Safety and Efficacy of Albuterol on Motor Function in Individuals With Late-onset Pompe Disease Receiving Enzyme Replacement Therapy Condition: Pompe Disease Date: 2013-06-21 Interventions:
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Recruiting |
Study Name: Muscle Response to Enzyme Replacement Therapy in Pompe Disease Condition: Pompe Disease Date: 2008-07-09 |
Recruiting |
Study Name: Response to Diaphragmatic Pacing in Subjects With Pompe Disease Condition: Pompe Disease Date: 2015-01-21 Interventions:
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Recruiting |
Study Name: Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies Condition: Pompe Disease Date: 2011-09-15 Interventions:
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Recruiting |
Study Name: Pompe Disease Registry Condition:
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Completed |
Study Name: Safety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe Disease Condition: Pompe Disease Date: 2009-07-13 Interventions:
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