Clinical Trial: A Retrospective, Observational, Noninterventional Data Collection Study for Patients With Molybdenum Cofactor Deficiency Who Have Been Previously Treated With Cyclic Pyranopterin Monophosphate (cPMP)
Study Status: Completed
Recruit Status: Completed
Study Type: Observational
Official Title: A Retrospective, Observational, Noninterventional Data Collection Study for Patients With Molybdenum Cofactor Deficiency Who Have Been Previously Treated With Cyclic Pyran
Brief Summary: The primary objective is to assess safety and efficacy data of Escherichia coli-derived cPMP in patients with molybdenum cofactor deficiency (MoCD).
Detailed Summary:
Sponsor: Alexion Pharmaceuticals
Current Primary Outcome: Safety and Efficacy [ Time Frame: For up to 60 months from the initial date of treatment with cPMP ]
Original Primary Outcome:
Current Secondary Outcome:
Original Secondary Outcome:
Information By: Alexion Pharmaceuticals
Dates:
Date Received: July 12, 2012
Date Started: November 2012
Date Completion:
Last Updated: February 17, 2016
Last Verified: February 2016